Lambert et al., 2020
- PDE10A inhibition reduces the manifestation of pathology in DMD zebrafish and represses the genetic modifier PITPNA.
Molecular therapy : the journal of the American Society of Gene Therapy
29(3):1086-1101
Full text @ Mol. Ther.
Marker Type | Symbol | Name |
---|---|---|
Gene | dmd | dystrophin |
Gene | hprt1 | hypoxanthine phosphoribosyltransferase 1 |
Gene | pde10a | phosphodiesterase 10A |
Gene | pitpnaa | phosphatidylinositol transfer protein, alpha a |