Lek et al., 2020
- Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy.
Science Translational Medicine
12(536)
Full text @ Sci. Transl. Med.
Human Disease | Fish | Environment | Evidence Code |
---|---|---|---|
facioscapulohumeral muscular dystrophy | cl102Tg | chemical treatment by environment: tamoxifen |