Lek et al., 2020 - Applying genome-wide CRISPR-Cas9 screens for therapeutic discovery in facioscapulohumeral muscular dystrophy. Science Translational Medicine   12(536) Full text @ Sci. Transl. Med.
Human Disease / Model Data (1 Record)
Human Disease Fish Environment Evidence Code
facioscapulohumeral muscular dystrophy cl102Tg chemical treatment by environment: tamoxifen