Hightower et al., 2019
- The SINE Compound KPT-350 Blocks Dystrophic Pathologies in DMD Zebrafish and Mice.
Molecular therapy : the journal of the American Society of Gene Therapy
28(1):189-201
Full text @ Mol. Ther.
Human Disease | Fish | Environment | Evidence Code |
---|---|---|---|
Duchenne muscular dystrophy | dmdta222a/ta222a | standard conditions |