Riessland et al., 2017
- Neurocalcin Delta Suppression Protects against Spinal Muscular Atrophy in Humans and across Species by Restoring Impaired Endocytosis.
American journal of human genetics
100(2):297-315
Full text @ Am. J. Hum. Genet.
Target | Reagent |
---|---|
ncaldb | MO1-ncaldb |
smn1 | MO1-smn1 |