Riessland et al., 2017 - Neurocalcin Delta Suppression Protects against Spinal Muscular Atrophy in Humans and across Species by Restoring Impaired Endocytosis. American journal of human genetics   100(2):297-315 Full text @ Am. J. Hum. Genet.
Morpholino List (2 Records)
Target Reagent
ncaldb MO1-ncaldb
smn1 MO1-smn1