Sabha et al., 2016 - PIK3C2B inhibition improves function and prolongs survival in myotubular myopathy animal models. The Journal of Clinical Investigation   126(9):3613-25 Full text @ Journal of Clin. Invest.
Morpholino List (2 Records)
Target Reagent
mtm1 MO3-mtm1
pik3c2b MO1-pik3c2b