Winkler et al., 2005 - Reduced U snRNP assembly causes motor axon degeneration in an animal model for spinal muscular atrophy. Genes & Development   19(19):2320-2330 Full text @ Genes & Dev.
Morpholino List (3 Records)
Target Reagent
clns1a MO1-clns1a
gemin2 MO1-gemin2
smn1 MO1-smn1