Winkler et al., 2005
- Reduced U snRNP assembly causes motor axon degeneration in an animal model for spinal muscular atrophy.
Genes & Development
19(19):2320-2330
Full text @ Genes & Dev.
Target | Reagent |
---|---|
clns1a | MO1-clns1a |
gemin2 | MO1-gemin2 |
smn1 | MO1-smn1 |